TreatSMA

Nusinersen patient Q&As

Patient organisations have asked for NICE and NHS to answer a few very important questions with regards to MAA and access to Nusinersen. We are now able to share their answers in the attached documents. We will continue to push for expanded access for this treatment to make sure that everybody gets a chance.

Both NICE and NHSE have published this information. NHSE are working on the access for adults guidance, and documents relating to the 3 remaining guides (about Nusinersen, the treatment process and data collection) will be published soon.

Spinraza access for children

MANAGED ACCESS AGREEMENT QA

MAA Data Collection

The Treatment Process

About Nusinersen

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