Scholar Rock Announce New 36-Month Apitegromab Extension Data
Scholar Rock have announced new 36-Month Apitegromab Extension Data which reinforces long-term substantial and sustained improvement of motor function in phase 2 Topaz trial patients…
UK campaign for access to treatments and support for those with spinal muscular atrophy
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Latest posts
Scholar Rock Announce New 36-Month Apitegromab Extension Data
Scholar Rock have announced new 36-Month Apitegromab Extension Data which reinforces long-term substantial and sustained improvement of motor function in phase 2 Topaz trial patients…
Join the NIHR online Q&A: severe neuromuscular diseases in children
On Wednesday 12th July 2023, 7pm to 8pm the National Institute for Health and Care Research, which supports delivery of research in the NHS, public health…
Join the NIHR online Q&A: severe neuromuscular diseases in children
On Wednesday 12th July 2023, 7pm to 8pm the National Institute for Health and Care Research, which supports delivery of research in the NHS, public health…
Physical ability: What is important to you? Take part
Are you interested in participating in two telephone/video interviews to discuss your experience of Spinal Muscular Atrophy (SMA) and to help us understand what an…
Physical ability: What is important to you? Take part
Are you interested in participating in two telephone/video interviews to discuss your experience of Spinal Muscular Atrophy (SMA) and to help us understand what an…
Despite their already reading treatments available the world of science never stops. They continues to be active trials and development on a number of new treatments. Below is the current position to the best of our knowledge of each, and this will be updated as we receive further updates