Support for the 6th March SMA Vigil
Support is available for the 6th March Manchester Vigil.
UK campaign for access to treatments and support for those with spinal muscular atrophy
What is sma?
A comprehensive guide to what SMA is
and what to be aware of.
Treatment information
Everything you need to know about treatments available now and future.
STANDARDS OF CARE
SMA experts have developed and published consensus guidelines on SMA care.
Latest posts
Updated TreatSMA press release on current developments
A TreatSMA press release on the current status of nusinersen (Spinraza®) appraisal.
A report names Spinraza as most high-profile case of “inflexible, inappropriate” approach to orphan drug appraisal
Spinraza has been called the most high-profile case of inflexible, inappropriate approach by NICE.
TreatSMA Vigil 6th March 2019
On 6th March, TreatSMA along with many families and adults from the SMA community will once again travel to Manchester for the 3rd appraisal meeting…
Eleanor Smith MP asks PM Theresa May about Spinraza
Eleanor Smith MP asked the Prime Minister about access to Spinraza during today’s PM Question Time.
I lay by my boy as he died at five months…
Paul and Jeanette narrate their struggle with spinal muscular atrophy in a recent edition of The Mirror.
Despite their already reading treatments available the world of science never stops. They continues to be active trials and development on a number of new treatments. Below is the current position to the best of our knowledge of each, and this will be updated as we receive further updates