Author: Andi Thornton
Questions and Answers session with Roche about Risdiplam
We joined a session with Roche earlier this week to ask them questions following their recent announcement about risdiplam. The following FAQs have been checked for accuracy with Roche where they relate specifically to risdiplam. Questions and answers apply to people living in England, Scotland, Northern Ireland and Wales.
SMA Awareness Month – MHRA Webinar
A really interesting webinar hosted by our very own Joseph talking to Dan from the MHRA about the regulatory process associated with rare diseases and their involvement in assessing suitability and helping licensing drugs.
Questions and Answers session with Roche about Risdiplam
We joined a session with Roche earlier this week to ask them questions following their recent announcement about risdiplam. The following FAQs have been checked for accuracy with Roche where they relate specifically to risdiplam. Questions and answers apply to people living in England, Scotland, Northern Ireland and Wales.
SMA Awareness Month – MHRA Webinar
A really interesting webinar hosted by our very own Joseph talking to Dan from the MHRA about the regulatory process associated with rare diseases and their involvement in assessing suitability and helping licensing drugs.
European Medicines Agency (EMA) has validated the Marketing Authorization Application (MAA) for Risdiplam.
European Medicines Agency (EMA) has validated the Marketing Authorization Application (MAA) for risdiplam for the proposed use in patients with spinal muscular atrophy (SMA).
SMA Awareness Month – Mary Bodzo on the amino acid Diet
Mary has become an expert and the go to person in the US with regards to the amino acid diet, something Mary used on her own daughter at the age of 5, and attributes the stability to of her condition to it. In this video Mary is interviewed by our very own Kelly as well…
SMA Awareness Month – Mary Bodzo on the amino acid Diet
Mary has become an expert and the go to person in the US with regards to the amino acid diet, something Mary used on her own daughter at the age of 5, and attributes the stability to of her condition to it. In this video Mary is interviewed by our very own Kelly as well…
SMA Awareness Month – Mariachristina webinar
We were fortunate enough to have one of the U.K.’s leading consultants in Spinal Muscular Atrophy to spend some time with us and the community to talk about SMA treatments as well as answer some questions.