Author: Andi Thornton
Nusinersen super effective in later-onset SMA!
Spinraza demostrated as incredibly effective in types 2 and 3 SMA
“Wear Your Hurt On Your Shirt” SMA Campaign
We are asking the SMA community, friends and family to wear in public on the 7th May a plain t-shirt or top with a personal message to NHS England and NICE telling them we will not wait any longer.
No commercial agreement yet. NICE to discuss Spinraza at another meeting
NICE has not yet been able to recommend Spinraza, and an urgent Committee meeting has been called.
Spinraza EAP opens in Russia
An Expanded Access Programme of Spinraza starts in Russia today.
NICE responds to us
NICE emailed us that they are not able to update us yet.
France decides to offer Spinraza to all
Today France authorised wide reimbursement of Spinraza. Everyone with SMA in the country will now have access to treatment.
NICE silence on Spinraza approval. TreatSMA demands action from NHS England
So I guess our silence is fairly obvious. We have heard nothing from NICE, not a single word.
AveXis discloses data on AVXS-101 efficacy in treating early onset spinal muscular atrophy
AVXS-101 shows amazing effects in treating spinal muscular atrophy.