Author: Marni Smyth
SMA Poland set up operation to help SMA families in Ukraine
This is a operation setup to help SMA families in Ukraine by SMA Poland. It went live this morning on the 27th February 2022. The link below has been shared with us, it has further details and has been written in Ukrainian. There is now a resource centre setup by SMA Poland for Ukrainian SMA…
Scottish NHS to Fund Risdiplam
We are so pleased to announce that the Scottish Medical Consortium has released its decision to fund Risdiplam for use on the NHS in Scotland to treat 5q SMA.
Managed Access Agreement (MAA) for Evrysdi (Risdiplam) for 5Q SMA type 1, 2 and 3.
We are so pleased to announce that NICE, NHS England and Roche have reached agreement on a Managed Access Agreement (MAA) for Evrysdi (Risdiplam) for children and adults with type 1, 2 and 3 SMA. The purpose of the MAA is to ensure access to treatment for the SMA community whilst further data is collected.…
TreatSMA on Tour – U.K.
It is becoming more apparent than ever that there is a lack of access to physiotherapists for children and adults in the community that specialise in SMA or have knowledge of and training in the condition.
Physio with Marion – ‘Choosing a private physiotherapist for you or your child (In the UK)’ document now available
The powerpoint slide Marion used in the latest episode of Physio with Marion titled Choosing a private physiotherapist for you or your child (In the UK) is now available as a PDF document.
Treatsma website reaches national news in Bhutan
Treatsma website reaches national news in Bhutan.
Update on Roche’s SMA global clinical development programme: New global combination study to begin in early 2022
We are pleased to share with you the initiation of MANATEE, a new global Phase 2/3 clinical study that aims to evaluate the safety and efficacy of GYM329 (RO7204239), an investigational anti-myostatin antibody targeting muscle growth in combination with risdiplam, in Spinal Muscular Atrophy (SMA).
Living with SMA – Hitting Our Fourties
TreatSMA Trustee Andi Thornton speaks with SMA UK Trustee Toby Mildon about mental health, treatments, University and work, health care and much more