Author: TreatSMA
Rexy’s Family
We were lucky with diagnosis, we’re looked after by a muscular dystrophy centre of excellence. Our team is very positive, we spoke about the need of future ventilation the importance of physio. We were told that it was an exciting time for SMA. Although this was great and we usually have a super positive outlook…
Nusinersen clinical trial update: Boy with type 1 SMA progressing well
This video from Nemours Children’s Hospital shows the effects of the drug nusinersen on a young spinal muscular atrophy (SMA) patient.