Author: TreatSMA
France decides to offer Spinraza to all
Today France authorised wide reimbursement of Spinraza. Everyone with SMA in the country will now have access to treatment.
NICE silence on Spinraza approval. TreatSMA demands action from NHS England
So I guess our silence is fairly obvious. We have heard nothing from NICE, not a single word.
AveXis discloses data on AVXS-101 efficacy in treating early onset spinal muscular atrophy
AVXS-101 shows amazing effects in treating spinal muscular atrophy.
Will NICE recommend Spinraza tomorrow?
We are all waiting for NICE’s decision on Spinraza which is planned for tomorrow.
A new clinical trial opens in presymptomatic babies
The Rainbowfish clinical trial of risdiplam has started.
Recruitment completed in branaplam trial
Recruitment to the branaplam trial has been completed.
Risdiplam trials: early results of Sunfish
Roche disclosed early data from part I of Sunfish trial – risdiplam
Risdiplam trials: exciting early results in Firefish
Roche disclosed early data from part I of Firefish trial – risdiplam