Author: TreatSMA
Spinraza approved in China
China approves nusinersen (Spinraza) to be used as a treatment for SMA.
Thousands demand Spinraza to be made available for adults in Croatia
Thousands protest in Croatia demanding wide access to Spinraza.
Turkey starts offering Spinraza to all
Starting 1st February, Turkey decided to offer Spinraza as a standard therapy to all people with SMA.
SMA families take to streets in Ireland to demand access to Spinraza
Hundreds of people took to streets in Dublin in protest against the continuous denial of Spinraza treatment by Irish health authorities.
Talking about SMA on Rare Disease Day
On Tuesday the 26th the TreatSMA team met the youth and talked about living with rare diseases.
Support for the 6th March SMA Vigil
Support is available for the 6th March Manchester Vigil.
Updated TreatSMA press release on current developments
A TreatSMA press release on the current status of nusinersen (Spinraza®) appraisal.
A report names Spinraza as most high-profile case of “inflexible, inappropriate” approach to orphan drug appraisal
Spinraza has been called the most high-profile case of inflexible, inappropriate approach by NICE.