UK campaign for access to treatments and support for those with spinal muscular atrophy
We have received notification that the Physical ability: What is important to you? The study has reached its quota for non-ambulant participants. As well as this they have extended the age range to 2-60 years old. Therefore, please see updated invitation below: Are you interested in participating in two telephone/video interviews to discuss your experience…
Today Biogen provided us with an update on the NURTURE study which was published in Muscle & Nerve1.
Spinal Muscular Atrophy (SMA) is a genetic condition that primarily impacts the motor neurons of the spinal cord. These neurons are vital for muscle activities such as crawling, walking, neck control, and even swallowing and breathing. SMA is characterized by a loss of motor neurons, which leads to muscle weakness and atrophy, or the wasting…
Scholar Rock have announced new 36-Month Apitegromab Extension Data which reinforces long-term substantial and sustained improvement of motor function in phase 2 Topaz trial patients with Nonambulatory SMA.
Scholar Rock have announced new 36-Month Apitegromab Extension Data which reinforces long-term substantial and sustained improvement of motor function in phase 2 Topaz trial patients with Nonambulatory SMA.
On Wednesday 12th July 2023, 7pm to 8pm the National Institute for Health and Care Research, which supports delivery of research in the NHS, public health and social care and Muscular Dystrophy UK, the UK charity for individuals and families living with muscle-wasting conditions are hosting a webinar where you can ask leading experts about the…
On Wednesday 12th July 2023, 7pm to 8pm the National Institute for Health and Care Research, which supports delivery of research in the NHS, public health and social care and Muscular Dystrophy UK, the UK charity for individuals and families living with muscle-wasting conditions are hosting a webinar where you can ask leading experts about the…
Are you interested in participating in two telephone/video interviews to discuss your experience of Spinal Muscular Atrophy (SMA) and to help us understand what an important change in physical ability would be?
Are you interested in participating in two telephone/video interviews to discuss your experience of Spinal Muscular Atrophy (SMA) and to help us understand what an important change in physical ability would be?
