Petition to get Newborn Screening funded immediately for Spinal Muscular Atrophy
A petition has been set up to get Newborn Screening funded immediately for Spinal Muscular Atrophy.
Category: Updates
NICE Release Statement on Risdiplam
Earlier today NICE released a statement regarding Risdiplam. NICE’s initial response is to say ‘no’ to funding Risdiplam.
NICE Release Statement on Risdiplam
Earlier today NICE released a statement regarding Risdiplam. NICE’s initial response is to say ‘no’ to funding Risdiplam.
Sibs: Camp in the Cloud for siblings and their families
A SMA community member has sent us the following information, they thought it would be useful for the SMA community.
Sibs: Camp in the Cloud for siblings and their families
A SMA community member has sent us the following information, they thought it would be useful for the SMA community.
Zolgensma Q&A
We have received further information from NHSE on Zolgensma. We will continue to update you all as we receive information. Please follow link below for the Q&A. Zolgensma Q and As
Zolgensma Q&A
We have received further information from NHSE on Zolgensma. We will continue to update you all as we receive information. Please follow link below for the Q&A. Zolgensma Q and As