A really interesting webinar hosted by our very own Joseph talking to Dan from the MHRA about the regulatory process associated with rare diseases and their involvement in assessing suitability and helping licensing drugs.
European Medicines Agency (EMA) has validated the Marketing Authorization Application (MAA) for risdiplam for the proposed use in patients with spinal muscular atrophy (SMA).
European Medicines Agency (EMA) has validated the Marketing Authorization Application (MAA) for risdiplam for the proposed use in patients with spinal muscular atrophy (SMA).
Mary has become an expert and the go to person in the US with regards to the amino acid diet, something Mary used on her own daughter at the age of 5, and attributes the stability to of her condition to it. In this video Mary is interviewed by our very own Kelly as well…
Mary has become an expert and the go to person in the US with regards to the amino acid diet, something Mary used on her own daughter at the age of 5, and attributes the stability to of her condition to it. In this video Mary is interviewed by our very own Kelly as well…
We were fortunate enough to have one of the U.K.’s leading consultants in Spinal Muscular Atrophy to spend some time with us and the community to talk about SMA treatments as well as answer some questions.
We were fortunate enough to have one of the U.K.’s leading consultants in Spinal Muscular Atrophy to spend some time with us and the community to talk about SMA treatments as well as answer some questions.
Dear Community TreatSMA has taken today to give remembrance to the Angels and the Warriors of the global SMA community tonight as we light a candle alongside you all to remember and make sure we never forget. In honour of those that lost their fight to SMA, the Trustees at Treatsma have each potted a…
