AveXis intrathecal trials halted after safety findings
The US Food and Drug Administration has suspended all clinical trials of AVXS-101 (Zolgensma®) gene therapy administered intrathecally due to safety findings in animals.
Category: Updates
First Physio with Marion session a great success – catch up here
TreatSMA hosted its first Physio with Marion session on Sunday, and thanks to Marion and all of those who took part in asking questions, it was a great success. You can catch up on a recording of the event above.
Physio with Marion – This Sunday
On the 27th October at 7pm TreatSMA is hosting a live webinar alongside physio Marion Main. This will be a regular slot at the end of each month. It can be viewed on all our social media platforms live and a recording will be put up on our website afterwards. Two topics will be covered…
Physio with Marion – This Sunday
On the 27th October at 7pm TreatSMA is hosting a live webinar alongside physio Marion Main. This will be a regular slot at the end of each month. It can be viewed on all our social media platforms live and a recording will be put up on our website afterwards. Two topics will be covered…
Early research suggests increased fat in the diet of SMA mouse model could harm liver function
As a part of our engagement with research into diet we came across this novel work and thought that general SMA population would be interested in the data.
Early research suggests increased fat in the diet of SMA mouse model could harm liver function
As a part of our engagement with research into diet we came across this novel work and thought that general SMA population would be interested in the data.
Gennadiy, Trustee for TreatSMA, secures position on Spinraza advisory panel
Our Trustee Gennadiy Ilyashenko has been accepted as a patient organisation representative on the Spinraza managed access oversight committee. This is fantastic news.
Gennadiy, Trustee for TreatSMA, secures position on Spinraza advisory panel
Our Trustee Gennadiy Ilyashenko has been accepted as a patient organisation representative on the Spinraza managed access oversight committee. This is fantastic news.