NICE refuses to recommend Spinraza to treat SMA
Shocking news. The National Institute of Health and Care Excellence officially recommends that nusinersen (Spinraza®) is NOT offered through the NHS to anyone with SMA.
Category: Updates
NICE refuses to recommend Spinraza to treat SMA
Shocking news. The National Institute of Health and Care Excellence officially recommends that nusinersen (Spinraza®) is NOT offered through the NHS to anyone with SMA.
AveXis gene therapy trial in UK
In the next few weeks we are expecting the AveXis AVXS-101 trial to start enrolling. There will be two site centres here in the UK: Great Ormond Street Hospital for Children Contact : hinal.patel@ucl.ac.uk The John Walton Muscular Dystrophy Research Centre MRC Centre for Neuromuscular Diseases. Contact: Anna.peel1@newcastle.ac.uk There will be strict inclusion and exclusion criteria…
AveXis gene therapy trial in UK
In the next few weeks we are expecting the AveXis AVXS-101 trial to start enrolling. There will be two site centres here in the UK: Great Ormond Street Hospital for Children Contact : hinal.patel@ucl.ac.uk The John Walton Muscular Dystrophy Research Centre MRC Centre for Neuromuscular Diseases. Contact: Anna.peel1@newcastle.ac.uk There will be strict inclusion and exclusion criteria…
August is SMA Awareness Month
It’s August and its SMA Awareness Month. Please take time to view and share our video. Lets TreatSMA in all its forms, and lets get more treatments as soon as we can to help all.
August is SMA Awareness Month
It’s August and its SMA Awareness Month. Please take time to view and share our video. Lets TreatSMA in all its forms, and lets get more treatments as soon as we can to help all.