A new trial of gene therapy in SMA announced
Today Avexis announced the start of a new clinical trial of gene therapy in SMA.
UK campaign for access to treatments and support for those with spinal muscular atrophy
BLOG ARCHIVE
SMA Awareness Day
Today 30/9 the world celebrates SMA Awareness Day. Do you know what SMA stands for?
A new trial of gene therapy in SMA announced
Today Avexis announced the start of a new clinical trial of gene therapy in SMA.
Spinraza will be offered in Italy to all with SMA
Yesterday the government in Rome decided that Spinraza will be offered in Italy to all those with spinal muscular atrophy.
Spinraza will be offered in Italy to all with SMA
Yesterday the government in Rome decided that Spinraza will be offered in Italy to all those with spinal muscular atrophy.
Important update on branaplam development programme
Another exciting update: branaplam, an experimental molecule for SMA from Novartis, is finally moving ahead.
First open TreatSMA meeting
On Moday 18 September TreatSMA families held a meetup in order to get updates about treatments and discuss actions needed for fast and broad access to SMA therapy in the UK.
Important update on branaplam development programme
Another exciting update: branaplam, an experimental molecule for SMA from Novartis, is finally moving ahead.
First open TreatSMA meeting
On Moday 18 September TreatSMA families held a meetup in order to get updates about treatments and discuss actions needed for fast and broad access to SMA therapy in the UK.